A toddler has been able to hear for the first time after being treated with a pioneering gene therapy for deafness. The child and her family live in the U.K. and were interviewed in this article by theThe girl has a hereditary mutation in a gene called otoferlin, an important part of allowing people to sense sound in the cells of the ear.
The therapy uses a genetically modified virus injected into a small area of the ear to fix the faulty gene "At 24 weeks, she has essentially normal hearing," said Lustig, noting that at higher frequencies of sound the child is still considered to have some mild loss of hearing ability.