Researchers publish final results of key clinical trial for gene therapy for sickle cell disease

  • 📰 medical_xpress
  • ⏱ Reading Time:
  • 46 sec. here
  • 7 min. at publisher
  • 📊 Quality Score:
  • News: 39%
  • Publisher: 51%

Medicine Research News News

Medicine Research,Health Research News,Health Research

In a landmark study, an international consortium led by researchers at Children's Hospital of Philadelphia (CHOP) published the final results of a key clinical trial of the gene therapy CASGEVY (exagamglogene autotemcel) for the treatment of sickle cell disease in patients 12 years and older with recurrent vaso-occlusive crises (VOCs).

Researchers publish final results of key clinical trial for gene therapy for sickle cell disease retrieved 25 April 2024 from https://medicalxpress.com/news/2024-04-publish-results-key-clinical-trial.html

This document is subject to copyright. Apart from any fair dealing for the purpose of private study or research, no part may be reproduced without the written permission. The content is provided for information purposes only.Jun 14, 2022Use this form if you have come across a typo, inaccuracy or would like to send an edit request for the content on this page. For general inquiries, please use ourThank you for taking time to provide your feedback to the editors.

Your feedback is important to us. However, we do not guarantee individual replies due to the high volume of messages.to let the recipient know who sent the email. Neither your address nor the recipient's address will be used for any other purpose. The information you enter will appear in your e-mail message and is not retained by Medical Xpress in any form.Get weekly and/or daily updates delivered to your inbox.

 

Thank you for your comment. Your comment will be published after being reviewed.
Please try again later.
We have summarized this news so that you can read it quickly. If you are interested in the news, you can read the full text here. Read more:

 /  🏆 101. in HEALTH

Health Health Latest News, Health Health Headlines

Similar News:You can also read news stories similar to this one that we have collected from other news sources.

Asthma in children: Researchers envision novel drug to reduce the risk of the diseaseScientists have reached a milestone in the research of childhood asthma. For the first time, they have clarified how a certain genetic defect in children initially leads to frequent infections and later to asthma.
Source: medical_xpress - 🏆 101. / 51 Read more »

Researchers uncover underlying mechanism driving membranous nephropathy, a chronic kidney disease in childrenNo therapies currently exist that can halt the progression of chronic kidney disease in children or restore the ability of kidney cells to filter blood.
Source: medical_xpress - 🏆 101. / 51 Read more »